We stand by the sides of families with no other option. The underdogs. The ones left behind.

We stand ready to see what they see, feel what they feel. We fight for a world for them with less suffering and restored promise for a better tomorrow.


Equal Access

All people, regardless of their race, location or the number of people that have their disease— should have no barriers to accessing medicine or testing.


Life Changing Medicines

We combine the best therapeutic development expertise with philanthropic funding to create a sustainable model that delivers accessible cures to patients in need.



We deliver Detection and Prevention education to create the potential for major health impact at low cost.



Driven to defeat lethal diseases and inspired by the hope of a better tomorrow.

Together, locked arm-in-arm with its for-profit colleagues and partners, we will be even more connected as one industry with one goal, to transform the lives of anyone suffering - anywhere in the world.


Alex Karnal

Chief Executive Officer

Driven by investments that defeat disease and save lives.

James Wilson, M.D., Ph.D. 

Chief Scientific Officer

Gene therapy pioneer and expert in AAV technology.

Lawrence Atinsky

COO & General Counsel

Finding innovative ways to address unmet medical needs.

Anshul Mangal

Chief Strategy Officer

Committed to advancing next-generation medicines.

Bryan Sendrowski

Chief Financial Officer

Putting patients above all else – always.


Alex Karnal

Founder & Chairman

James Wilson, M.D., Ph.D. 

Founder & Board Member

Tachi Yamada, M.D.

Founder & Board Member

Judith Lea Swain, M.D

Board Member

Monique Molloy

Board Member

Julian Harris, M.D.

Board Member